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Muscle biopsies in clinical trials for Duchenne muscular dystrophy – Patients’ and caregivers’ perspective

Verhaart IEC, Johnson A, Thakrar S, et al. Muscle biopsies in clinical trials for Duchenne muscular dystrophy – Patients’ and caregivers’ perspective. Neuromuscular disorders : NMD 2019;29:576-584   Abstract The number of clinical trials for Duchenne muscular dystrophy is increasing. Many trials require muscle biopsies, which involve an invasive surgical procedure. Little is known about […]