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Overview of idebenone (SNT-MC17; Raxone; Puldysa) clinical trials

Trial publications Phase IIa placebo controlled study (NCT00654784) and open label extension study (NCT00758225) Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy (DELPHI) Long-term Safety, Tolerability and Efficacy of Idebenone in Duchenne Muscular Dystrophy (DELPHI Extension) Buyse GM, Goemans N, van den Hauwe M, et al. Idebenone as […]